Effectiveness of voxelotor in individuals with sickle cell disease and a history of red blood cell transfusions: A non-interventional, retrospective cohort study using real-world data in the United States

31/07/2024
07/04/2025
EU PAS number:
EUPAS1000000225
Study
Finalised
Documents
Study protocol
Initial protocol
English (766.55 KB - PDF) View document
Updated protocol
English (19.48 MB - PDF) View document
Study results
Study report
Study report
English (10.44 MB - PDF) View document
Other information