Effectiveness of voxelotor in individuals with sickle cell disease and a history of red blood cell transfusions: A non-interventional, retrospective cohort study using real-world data in the United States

First published 31/07/2024

Last updated 07/04/2025

EU PAS number:

EUPAS1000000225

Study

Finalised

Documents

Study protocol

Initial protocol

C5341060_Pfizer_Oxbryta Reduction in Transfusion Study Protocol_PASS_V2.0_23Dec2024 _Redacted.pdf

English (766.55 KB - PDF)View document

Updated protocol

C5341060_Pfizer_Oxbryta Reduction in Transfusion Study_Protocol_V2.1_09Jan2025_Redacted.pdf

First published: 06/03/2025

English (19.48 MB - PDF)View document

Study results

Study report

C5341060 -Interventional-Low-Interventional Study Type Study Report Redacted.pdf

English (10.44 MB - PDF)View document

Other information

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