Effectiveness of voxelotor in individuals with sickle cell disease and a history of red blood cell transfusions: A non-interventional, retrospective cohort study using real-world data in the United States

31/07/2024
07/04/2025
EU PAS number:
EUPAS1000000225
Study
Finalised
Data sources

Data source(s), other

Optum Electronic Health Records and Claims Data, Komodo’s Healthcare Map (KHM) database, Claritas prescription data, Quest Diagnostics lab data
Use of a Common Data Model (CDM)

CDM mapping

No
Data quality specifications

Check conformance

Yes

Check completeness

Yes

Check stability

Yes

Check logical consistency

Yes
Data characterisation

Data characterisation conducted

Yes

Data characterisation moment

after data extraction