Long-term registry-based study of patients with transfusion-dependent β-thalassemia (TDT) or sickle cell disease (SCD) treated with exagamglogene autotemcel (exa-cel)First published 12/03/2025 Last updated 12/03/2025 EU PAS number: EUPAS1000000504StudyPlanned
Center for International Blood and Marrow Transplant Research (CIBMTR) First published: 01/02/2024Last updated 01/02/2024 Institution
European Society for Blood and Marrow Transplantation (EBMT)European Union First published: 20/02/2024Last updated 20/02/2024 Institution
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