Long-term registry-based study of patients with transfusion-dependent β-thalassemia (TDT) or sickle cell disease (SCD) treated with exagamglogene autotemcel (exa-cel)

12/03/2025
11/02/2026
EU PAS number:
EUPAS1000000504
Study
Ongoing

ENCePP Code of conduct

No information provided.
Data sources

Data source(s), other

European Society for Blood and Marrow Transplantation (EBMT) Registry
Center for International Blood and Marrow Transplant Research (CIBMTR) Registry

Use of a Common Data Model (CDM)

CDM mapping

No
Data quality specifications

Check conformance

Unknown

Check completeness

Unknown

Check stability

Unknown

Check logical consistency

Unknown
Data characterisation

Data characterisation conducted

Unknown
Procedures
No information provided.