Long-term registry-based study of patients with transfusion-dependent β-thalassemia (TDT) or sickle cell disease (SCD) treated with exagamglogene autotemcel (exa-cel)

12/03/2025
11/02/2026
EU PAS number:
EUPAS1000000504
Study
Ongoing
Data sources

Data source(s), other

European Society for Blood and Marrow Transplantation (EBMT) Registry
Center for International Blood and Marrow Transplant Research (CIBMTR) Registry

Use of a Common Data Model (CDM)

CDM mapping

No
Data quality specifications

Check conformance

Unknown

Check completeness

Unknown

Check stability

Unknown

Check logical consistency

Unknown
Data characterisation

Data characterisation conducted

Unknown