An Observational Cohort Study to Assess Long-Term Safety of Danicopan Add-on Therapy in Patients with Paroxysmal Nocturnal Hemoglobinuria: Analysis of IPIG-Registry Data

17/12/2025
17/12/2025
EU PAS number:
EUPAS1000000876
Study
Planned
Documents
Study protocol
Updated protocol
English (1.89 MB - PDF) View document
Study results
Study report
Other information