Description and assessment of fitness-for-purpose of real-world data (RWD) sources on Duchenne Muscular Dystrophy for regulatory decision-making

26/09/2025
05/03/2026
EU PAS number:
EUPAS1000000748
Study
Ongoing
Documents
Study protocol
Study results
Study report
Abstract of study report
English (454.16 KB - PDF) View document
Other information