Retrospective and prospective observational study on the systemic outcomes of lysosomal storage diseases with skeletal involvement in their natural history or during standard of care treatment

Data sources

• Data source(s), other:
  Patients clinical charts

Use of a Common Data Model (CDM)

• CDM mapping:
  No

Data quality specifications

• Check conformance:
  Unknown
• Check completeness:
  Unknown
• Check stability:
  Unknown
• Check logical consistency:
  Unknown

Data characterisation

• Data characterisation conducted:
  No