Healthcare Professional (HCP) Survey to Assess the Effectiveness of the Additional Risk Minimization Measures (aRMM) for Casgevy® (exagamglogene autotemcel)

08/08/2025
08/08/2025
EU PAS number:
EUPAS1000000704
Study
Planned
Data sources

Data source(s), other

The data source will be surveys completed by HCPs who have counseled patients regarding Casgevy as a treatment option at ATCs.

Data sources (types)

Other

Data sources (types), other

Health Care Provider survey
Use of a Common Data Model (CDM)

CDM mapping

No
Data quality specifications

Check conformance

Unknown

Check completeness

Unknown

Check stability

Unknown

Check logical consistency

Unknown
Data characterisation

Data characterisation conducted

Unknown