A European, non-interventional, multicentre, registry-based post-authorisation safety study to evaluate the long-term safety of Loargys treatment in arginase 1 deficiency patients in standard clinical care

07/07/2025
07/07/2025
EU PAS number:
EUPAS1000000555
Study
Planned
Documents
Study protocol
Initial protocol
English (596.15 KB - PDF) View document
Study results
Study report
Other information