A Retrospective Data Collection and Analysis Study of Patients With Sickle Cell Disease (SCD) Who Have Been Treated With Oxbryta® (Voxelotor)

14/10/2024
14/10/2024
EU PAS number:
EUPAS1000000334
Study
Ongoing

ENCePP Code of conduct

N/A
Data sources

Data source(s), other

Rutgers Cancer Institute of New Jersey
Brigham and Women's Hospital
Montefiore Medical Center
Central Michigan University/Children's Hospital of Michigan
UT Southwestern Medical Center
Levine Cancer Institute
Duke University Hospital
University of Connecticut Health
University of Texas Health Science Center at Houston

Data sources (types)

Non-interventional study
Use of a Common Data Model (CDM)

CDM mapping

No
Data quality specifications

Check conformance

Yes

Check completeness

Yes

Check stability

Yes

Check logical consistency

Yes
Data characterisation

Data characterisation conducted

Unknown