Study identification

PURI

https://redirect.ema.europa.eu/resource/1000000296

EU PAS number

EUPAS1000000296

Study ID

1000000296

Official title and acronym

Prospective, Registry-Based Observational Cohort Study of Ritlecitinib Safety in Pregnancy

DARWIN EU® study

No

Study countries

United States

Study description

Research question: Is there an increased risk of adverse maternal and/or infant outcomes in individuals with AA exposed to ritlecitinib during pregnancy?
Primary objective: To estimate the prevalence of major congenital malformation [MCM] births (primary outcome) among pregnant individuals with alopecia areata [AA] who are (1) exposed to ritlecitinib (exposed cohort) and (2) unexposed to ritlecitinib (comparator cohort).
Secondary objectives: 1. To estimate the prevalence of the following secondary outcomes in the 2 cohorts: SAB, elective termination, pregnancy complications (pre-eclampsia, eclampsia), stillbirth, preterm birth, SGA, minor congenital malformation, infant postnatal growth deficiency, and infant developmental delay. 2. To estimate the RR of each of the study outcomes in the exposed versus unexposed cohorts, if sample size permits.
Study design: This registry-based, prospective observational cohort study will enroll and follow pregnant individuals in the US, including individuals with AA exposed to ritlecitinib during pregnancy and individuals with AA unexposed to ritlecitinib during pregnancy. This study will be a new, product-based pregnancy registry. Participation in the registry is voluntary and participants can withdraw their consent to participate at any time. Data will be collected from enrolled pregnant individuals and the HCPs involved in their care or the care of their infants.
The primary study outcome is MCM and the secondary outcomes are SAB, elective termination, pregnancy complications (pre-eclampsia, eclampsia), stillbirth, preterm birth, SGA, minor congenital malformation, postnatal growth deficiency, and infant developmental delay. The main measures of effect are the prevalence of each outcome in the 2 study cohorts and, if sample size permits, the RR of each outcome, comparing the cohorts.


Study status

Planned
Research institutions and networks

Institutions

Pfizer
First published:
01/02/2024
Institution

Contact details

Monica Bertoia

Primary lead investigator
Study timelines

Date when funding contract was signed

Planned:
Actual:

Study start date

Planned:

Data analysis start date

Planned:

Date of interim report, if expected

Planned:

Date of final study report

Planned:
Sources of funding
Pharmaceutical company and other private sector 

More details on funding

Pfizer 100%
Study protocol
Initial protocol
English (813.28 KB - PDF)View document
Regulatory

Was the study required by a regulatory body?

Yes

Is the study required by a Risk Management Plan (RMP)?

Non-EU RMP only