A Two-Part, International, Real-World, Observational Registry of Participants Diagnosed with Aromatic L-Amino Acid Decarboxylase Deficiency (AADC-d) With or Without Treatment With Eladocagene Exuparvovec (PTC-AADC-MA-406)

16/06/2023
25/06/2025
EU PAS number:
EUPAS105422
Study
Ongoing
Documents
Study protocol
Study results
Study report
Other information