GENEr8-GTR: A Retrospective Cohort Study of Patients Treated with ROCTAVIAN™ (valoctocogene roxaparvovec): An Analysis of Patient Registries (BMN 270-801)

ENCePP Code of conduct

No

Data sources

• Data source(s):
  The World Federation of Hemophilia Gene Therapy Registry
• Data source(s), other:
  - American Thrombosis and Hemostasis Network (ATHN), United States; - EUHASS - Blood disorders
• Data sources (types):
  Disease registry

Use of a Common Data Model (CDM)

• CDM mapping:
  No

Data quality specifications

• Check conformance:
  Unknown
• Check completeness:
  Unknown
• Check stability:
  Unknown
• Check logical consistency:
  Unknown

Data characterisation

• Data characterisation conducted:
  No