Evaluation of referring HCPs’ and parents’/carers’ understanding of specific risks associated with Strimvelis™ treatment (STRIM-001)

21/07/2017
11/03/2024
EU PAS number:
EUPAS19951
Study
Finalised

ENCePP Code of conduct

No
Data sources

Data sources (types)

Patient surveys
Use of a Common Data Model (CDM)

CDM mapping

No
Data quality specifications

Check conformance

Unknown

Check completeness

Unknown

Check stability

Unknown

Check logical consistency

Unknown
Data characterisation

Data characterisation conducted

No