Adenosine Deaminase Severe Combined Immunodeficiency (ADA-SCID) Registry for Patients Treated with Strimvelis (or GSK2696273) Gene Therapy: Long-Term Prospective, Non-Interventional Follow-up of Safety and Effectiveness (STRIM-003)

19/01/2017
06/11/2025
EU PAS number:
EUPAS15795
Study
Ongoing
Documents
Study protocol
Study results
Study report
Other information