Long-Term Observational study of Translarna Safety and Effectiveness in Usual Care (STRIDE)

Documents

Study protocol

Study results

Study report

Other information

Publications

Study publications

Muntoni F, Desguerre I, Guglieri M, Osorio AN, Kirschner J, Tulinius M, Buccell…

Mercuri E, Muntoni F, Osorio AN, Tulinius M, Buccella F, Morgenroth LP, Gordish…