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Long-Term Observational study of Translarna Safety and Effectiveness in Usual Care (STRIDE)

13/10/2015
17/04/2025
EU PAS number:
EUPAS11275
Study
Ongoing
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Muntoni F, Desguerre I, Guglieri M, Osorio AN, Kirschner J, Tulinius M, Buccell…
Mercuri E, Muntoni F, Osorio AN, Tulinius M, Buccella F, Morgenroth LP, Gordish…

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