Paroxysmal Nocturnal Hemoglobinuria (PNH) Registry (M07-001)

Documents

Study protocol

Initial protocol

M07-001 Am 7_Final_18Jan2019 SIGNED_PG and PDV

Study results

No information provided.

Study report

No information provided.

Publications

Study publications

Lee JW, et al. Effectiveness of eculizumab in patients with paroxysmal nocturna…

Schrezenmeier H, et al. Baseline clinical characteristics and disease burden in…

Röth A, et al. Screening and diagnostic clinical algorithm for paroxysmal noctu…

Röth A, et al. Beneficial effects of eculizumab regardless of prior transfusion…

Höchsmann B, et al. Effect of Eculizumab Treatment in Patients with Paroxysmal …

ENCePP Seal

The use of the ENCePP Seal has been discontinued since February 2025. The ENCePP Seal fields are retained in the display mode for transparency but are no longer maintained.

No information provided.