A Post-Authorization, Multicenter, Multinational, Longitudinal, Observational Safety Registry Study for Patients Treated with Voretigene Neparvovec

First published 29/08/2019

Last updated 25/09/2025

EU PAS number:

EUPAS31153

Study

Ongoing

Documents

Study protocol

Initial protocol

LTW888A12401 PASS Protocol_July 2019_Redacted_21 Aug 2019

English (861.51 KB - PDF) View document

Updated protocol

Protocol Amendment_-_V03_Redacted_09 Jun 2025.pdf

First published: 22/09/2025

English (650.46 KB - PDF) View document

CLTW888A12401-v02--protocol_Redacted

First published: 22/02/2024

English (980.31 KB - PDF) View document

Study results

Study report

Other information

Secondary tabs