A Prospective, Long-Term Registry of Patients with a Diagnosis of Spinal Muscular Atrophy (SMA) - (RESTORE)

27/08/2021
03/09/2024
EU PAS number:
EUPAS41853
Study
Ongoing
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Documents
Study protocol
Initial protocol

PRO-1300 RESTORE AVXS-101-RG-001_Redacted

English (1.75 MB - PDF) View document
Updated protocol

PMA1234_RESTORE Protocol Amendment 3.0_V4.0 final_Redacted.pdf

First published: 08/05/2024
English (784.1 KB - PDF) View document
Study results
Study report
Other information