THE ALPHA-MANNOSIDOSIS REGISTRY: A multi-centre, multi-country, non interventional, prospective cohort, in alpha-mannosidosis patients (SPARKLE)

22/03/2019
02/07/2024
EU PAS number:
EUPAS29038
Study
Ongoing
Documents
Study protocol
Initial protocol
English (566.24 KB - PDF) View document
Updated protocol
English (537.25 KB - PDF) View document
Study results
Study report
Other information